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Spinal muscular atrophy
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About this condition
Spinal muscular atrophy (SMA) is a rare genetic disorder that affects the nerves controlling muscle movement, leading to muscle weakness and wasting. It occurs when the body lacks a protein needed for nerve cell survival. Symptoms can range from mild to severe and may include difficulty walking, breathing, and swallowing. Treatments such as gene therapy, medications, and physical therapy can help improve mobility, slow disease progression, and enhance quality of life.
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