
Gaucher disease
·
Inclusion of Gaucher disease in newborn screening panels across the U.S.
Apr 9, 2025

Hemophilia
·
Qfitlia: A breakthrough in hemophilia treatment
Apr 3, 2025

Multiple myeloma
·
Navigating clinical trials in multiple myeloma
Apr 2, 2025

Gene and cell therapy
·
An introduction to cell therapy
Mar 25, 2025

Gene and cell therapy
·
An introduction to gene therapy
Mar 19, 2025

Amyotrophic lateral sclerosis
·
A guide to nutrition for patients with amyotrophic lateral sclerosis
Feb 26, 2025

Huntington's disease
·
A guide to nutrition for patients with Huntington's disease
Feb 26, 2025

Spinal muscular atrophy
·
A guide to nutrition for patients with spinal muscular atrophy
Feb 26, 2025

Multiple myeloma
·
A guide to nutrition for patients with multiple myeloma
Feb 26, 2025

Hemophilia
·
A guide to nutrition for patients with hemophilia
Feb 26, 2025

Primary biliary cholangitis
·
A guide to nutrition for patients with primary biliary cholangitis (PBC)
Feb 19, 2025

Duchenne muscular dystrophy
·
A guide to nutrition for patients with Duchenne muscular dystrophy
Feb 19, 2025

Friedreich's ataxia
·
A guide to nutrition for patients with Friedreich's ataxia
Feb 19, 2025

Sickle cell
·
A guide to nutrition for patients with sickle cell
Feb 19, 2025

Mantle cell lymphoma
·
A guide to nutrition for patients with mantle cell lymphoma
Feb 19, 2025

Myasthenia gravis
·
A guide to nutrition for patients with myasthenia gravis
Feb 19, 2025

Primary biliary cholangitis
·
Specialty pharmacies: a guide for primary biliary cholangitis patients & carers
Feb 12, 2025

Myasthenia gravis
·
Specialty pharmacies: a guide for myasthenia gravis patients & carers
Feb 12, 2025

Mantle cell lymphoma
·
Specialty pharmacies: a guide for mantle cell lymphoma patients & carers
Feb 12, 2025

Friedreich's ataxia
·
Specialty pharmacies: a guide for Friedreich’s ataxia patients & carers
Feb 12, 2025

Duchenne muscular dystrophy
·
Specialty pharmacies: a guide for Duchenne muscular dystrophy patients & carers
Feb 12, 2025

Spinal muscular atrophy
·
Specialty pharmacies: a guide for SMA patients & carers
Feb 6, 2025

Sickle cell
·
Specialty pharmacies: a guide for sickle cell patients & carers
Feb 6, 2025

Multiple myeloma
·
Specialty pharmacies: a guide for multiple myeloma patients & carers
Feb 6, 2025

Huntington's disease
·
Specialty pharmacies: a guide for Huntington’s disease patients & carers
Feb 6, 2025

Hemophilia
·
Specialty pharmacies: a guide for hemophilia patients & carers
Feb 6, 2025

Amyotrophic lateral sclerosis
·
Specialty pharmacies: a guide for ALS patients & carers
Feb 6, 2025

Duchenne muscular dystrophy
·
Understanding Duchenne muscular dystrophy: a guide for patients
Jan 30, 2025

Friedreich's ataxia
·
Understanding Friedreich's ataxia: a guide for patients
Jan 30, 2025

Hemophilia
·
Understanding hemophilia: a guide for patients
Jan 30, 2025

Huntington's disease
·
Understanding Huntington’s disease: a guide for patients
Jan 30, 2025

Multiple myeloma
·
Understanding multiple myeloma: a guide for patients
Jan 30, 2025

Primary biliary cholangitis
·
Understanding primary biliary cholangitis: a guide for patients
Jan 30, 2025

Spinal muscular atrophy
·
Understanding spinal muscular atrophy: a guide for patients
Jan 30, 2025

Amyotrophic lateral sclerosis
·
Understanding amyotrophic lateral sclerosis: a guide for patients
Jan 23, 2025

Mantle cell lymphoma
·
What is mantle cell lymphoma? A guide to MCL and common medical terms
Jan 23, 2025

Myasthenia gravis
·
Understanding myasthenia gravis: a guide for patients
Jan 23, 2025

Sickle cell
·
Understanding sickle cell disease: a guide for patients
Jan 23, 2025

Primary biliary cholangitis
·
Exploring financial assistance options for primary biliary cholangitis treatment in the U.S.
Jan 17, 2025

Spinal muscular atrophy
·
Understanding financial pathways: support and resources for SMA treatment in the U.S.
Jan 17, 2025

Duchenne muscular dystrophy
·
Financial strategies for muscular dystrophy in the U.S.
Jan 17, 2025

Hemophilia
·
Navigating financial assistance for hemophilia treatment in the U.S.
Jan 17, 2025

Multiple myeloma
·
Unlocking support: a guide to financial and insurance resources for multiple myeloma patients
Jan 17, 2025

Friedreich's ataxia
·
Navigating Friedreich’s ataxia in the U.S.: a practical guide to support and financial planning
Jan 17, 2025

Mantle cell lymphoma
·
Diagnosis to empowerment: questions to ask and steps to take after being diagnosed with MCL
Jan 16, 2025

Amyotrophic lateral sclerosis
·
Finding joy and purpose in the face of ALS
Jan 16, 2025

Sickle cell
·
Thriving through the challenges: tips for managing school, work, and family with sickle cell disease
Jan 16, 2025

Myasthenia gravis
·
Financial strategies for living with myasthenia gravis in the U.S.: a guide to long-term planning
Jan 16, 2025